Oral presentation highlights novel compact RT editor demonstrating first preclinical in vivo proof of concept for precise ...

Gene editing history will have a lot to say about 2021. That year, two in vivo CRISPR-based therapies showed promise in human trials. One of the therapeutics, from Intellia Therapeutics and Regeneron ...

Vascular endothelial cells serve as a protective barrier in blood-vessel walls and serve as an active source for the synthesis, metabolism, uptake, storage, and degradation of a number of vasoactive ...

Please provide your email address to receive an email when new articles are posted on . An experimental gene editing cell therapy for sickle cell disease has shown encouraging early results in a phase ...

Researchers restored hearing in preclinical mouse models with a specific form of inherited deafness called DFNA50 caused by mutations in microRNA, by using a novel in vivo CRISPR genome editing ...

A single injection of a novel CRISPR gene-editing treatment safely and efficiently removes SIV -- a virus related to the AIDS-causing agent HIV -- from the genomes of non-human primates, scientists ...

Life Edit to receive upfront cash payment, research, and preclinical funding, and is eligible to receive milestone payments with tiered royalties on global net product sales CAMBRIDGE, MA and DURHAM, ...