A study showed that base editing can repair mutations linked to a rare liver disease. The therapy restored liver and cellular ...

Now, following up on that success, a large Chinese collaboration has followed up with a description of an improved gene ...

In 2025, baby KJ Muldoon became the first person to receive a personalized gene editing treatment, which likely saved his ...

The only gene-editing therapy approved for beta-thalassaemia at present is Vertex Pharma's CRISPR-based Casgevy ...

Using base editing, researchers targeted a genetic mutation linked to severe epilepsy. The approach reduced seizures and ...

University of Virginia School of Medicine scientists have used a next-generation form of gene editing to fix the underlying cause of a severe form of epilepsy in lab mice.

Scientists have corrected an extremely rare and life-threatening genetic disease of the liver in mouse models and human ...

In patients with sickle cell disease treated with ristoglogene autogetemcel, mean anti-sickling fetal hemoglobin levels were above 60% with a mean durable reduction in corresponding sickle hemoglobin ...

A domestically developed gene-editing therapy has successfully treated patients with beta-thalassemia, allowing them to live ...

Since 2017, a personalized immunotherapy called Chimeric Antigen Receptor, or CAR-T cell treatment, has worked wonders to ...

A domestically developed gene-editing therapy has successfully treated patients with beta-thalassemia, allowing them to live without the need for lifelong blood transfusions, according to a study ...

Add Yahoo as a preferred source to see more of our stories on Google. Futuristic 3D cubes showing DNA base pairs and a double helix. (Getty Images) This story was originally published on BioPharma ...